Tag: sickle cell disease
She cured her disease but she still is in pain
A team of US researchers has claimed they’ve transplanted the first gene therapy in sickle cell disease patients with only partially matched stem cells from a parent. The study, published in the journal Blood, also found that stem cells from only partly matched donors were able to be transplanted successfully in people with sickle-cell disease who received chemotherapy before the procedure.
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The FDA approved the first treatment for a human illness
Victoria Gray, a sickle cell patient who was the first person to receive CRISPR gene-editing treatment in the US, said she is “excited about the promise that this technology has for those living with sickle cell disease.” “Many of the countries where most sickle cell patients live don’t have enough sophisticated medical centres to provide the complicated treatment,” she added.
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